FARA's CEO, Jen Farmer, was honored to speak about the #FriedreichAtaxia #NaturalHistory study and it's important role in advancing therapies as we work to #CureFA . Thanks to Foundation for FDA for facilitating this valuable discussion.

FARA and Muscular Dystrophy Association are proud to announce a collaborative grant for $300,000 awarded to a team of investigators at UMass Chan Medical School. This funding will further research into using novel genetic technologies to treat #FriedreichsAtaxia (FA). Learn more: curefa.org/news-press-rel…

Last week, FARA's CEO, Director of Clinical Operations, & Director of Global Relations visited some of the FA GCC sites in Europe. The FA GCC is an international group of clinical research centers that work together to advance treatments & clinical care for individuals with FA.

How early does FA start impacting the body? We are excited to award a grant to Lucie Hermet at InstitutNeuroMyoGène to investigate the impact of FA on DRG and spinal cord formation and maturation that occurs during embryonic development and early in life.

Larimar Therapeutics Reports Positive Top-line Data from Phase 2 Dose Exploration Study from 25 mg and 50 mg Cohorts of Nomlabofusp in Patients with #FriedreichAtaxia

Click here to read their full press release: bit.ly/49bTrlc

We are excited to award a Graduate Research Fellowship to Shweta Sahni at All India Institute of Medical Sciences (AIIMS) in New Delhi to explore blood-based biomarkers of inflammation in Friedreich's ataxia (FA).

You can now access and view the recording of the Pediatric Research Initiatives in FA webinar on our YouTube channel!

▶️ Watch the Webinar: youtu.be/vrmRQTJl350

We are excited to share a discount code for Uplifting Athletes’s upcoming Young Investigator Draft on Feb. 3! Join us as we award Anusha Sivakumar with a $20,000 grant!

Use code: RARE35 at checkout for 35% off your ticket price! bit.ly/47R9QLz

The FDA drug label for SKYCLARYS has been updated (2.2).

Full prescribing information here: skyclarys.com/docs/skyclarys…

Anyone considering medication should discuss the matter with their physician. FARA does not endorse or recommend any particular medication.

Did you know that advancing understanding of cardiac disease in FA is a #FARAGrantProgram priority?

LOIs are due Feb. 15. curefa.org

Do you have ideas that will advance our understanding of the #neuroscience systems in #FriedreichAtaxia ? This is a priority of the #FARAGrantProgram , and funding is available. LOIs for general grants are due Feb. 15.

curefa.org/grant

Together, we will #CureFA

Advancing drug discovery is a priority of the #FARAGrantProgram .

Apply for funding to develop effective therapies for FA. Priority will be given to genetic, epigenetic, and protein replacement approaches that increase frataxin levels.

LOIs due Feb. 15.www.curefa.org/grant

We are excited to announce our collaboration with Uplifting Athletes to award Anusha Sivakumar a $20k grant in support of her research on Friedreich's ataxia! Join us in celebrating Dr. Sivakumar at the Young Investigator Draft on Feb 3! #YID24 bit.ly/47R9QLz

Facilitating the drug development process and translational research is a top priority of the #FARAGrantProgram .

LOIs are due Feb. 15. curefa.org/grant

Together, we will #SlowStopReverse and #CureFA !

Did you know that advancing understanding of the molecular basis of FA is a priority of the #FARAGrantProgram ?

Apply for funding for research. LOIs due Feb. 15. curefa.org/grant

Together, we will #SlowStopReverse and #CureFA !

Wishing you a brilliant new year, filled with inspiration to advance understanding and therapies for #FriedreichAtaxia . Funding is available through the #FARAGrantProgram .

curefa.org/Grant
AIM due Feb. 1.
LOIs for General Research Grants are due Feb. 15.

#CureFA !

Happy New Year 2024! May the year ahead be filled with love, laughter, and funding from the #FARAGrantProgram .

Learn more at curefa.org/Grant.
Applications for the Award for Innovative Mindset (AIM) due Feb. 1.
LOIs for General Grants are Feb. 15.

How will you celebrate the new year? Apply today for funding from the #FARAGrantProgram !

Learn more about funding opportunities at curefa.org/Grant
Applications for the Award for Innovative Mindset (AIM) due Feb. 1.
LOIs for General Research Grants due Feb. 15.

#CureFA !

Novel intragenic deletion within the FXN gene in a patient with typical phenotype of Friedreich ataxia: may be more prevalent than we think?
pubmed.ncbi.nlm.nih.gov/38041144/

Together, we will #CureFA !

Recent progress and applications of small molecule inhibitors of Keap1-Nrf2 axis for neurodegenerative diseases
pubmed.ncbi.nlm.nih.gov/38043492/

Together, we will #CureFA .